Home This week in gene and cell therapy - 22 June 2018 Gene and cell therapy headlines 15 - 22 June bluebird bio presents data from Phase 1/2 trial of LentiGlobin gene therapy for thalassemia and prepares for registration in Europe Chiesi granted FDA orphan drug designation for GPLSCD01 cell therapy for limbal stem cell deficiency (LSCD) Cellectis joins movement towards off the shelf CAR-T cell therapies Sarepta phase 1/2 trial of gene therapy for Duchenne muscular dystrophy shows promising early results