Home This week in gene and cell therapy - 13 July 2018 Gene and cell therapy headlines 9 - 13 July Axovant announces licensing of Benitec Silence and Replace and plans for 2019 oculopharyngeal muscular dystrophy clinical trial Non-cutting CRISPRa used to create iPS cells from fibroblasts Lysine derivative developed as an in vivo off switch for CRISPR/Cas FGF21 gene therapy for diabetes type 2 successful in mice Gene editing effective for controlling cholesterol in primates Pluristem Therapeutics and Thermo Fisher Scientific announce partnership to scale up cell