Home This week in gene and cell therapy - 31 August 2018 Gene and cell therapy headlines 27 - 31 August MeiraGTx' AAV-CNGA3 gene therapy for achromatopsia granted rare pediatric disease designation CAR-T news: Novartis' Kymriah and Gilead's Yescarta approved by EMA, but UK's National Health Service rejects Yescarta as too expensive bluebird bio and Gritstone Oncoloy announce partnership to develop cell therapy Gene therapy effective and safe in rat model of epilepsy Adverum's ADVM-022 gene therapy for macular degeneration granted investigational new drug status Exon skipping gene therapy for Duchenne muscular dystrophy effective in dogs